Advancing Therapies for Rare Diseases Act is Introduced

NORD supports this bipartisan bill, introduced in the US Senate, to advance the development of targeted drugs for patients with serious or life-threatening rare genetic diseases. The bill is intended to maintain FDA’s strong safety and effectiveness standards, while clarifying the agency’s authority to consider research supporting previously approved targeted treatments. More information.

NORD supports this bipartisan bill, introduced in the US Senate, to advance the development of targeted drugs for patients with serious or life-threatening rare genetic diseases. The bill is intended to maintain FDA’s strong safety and effectiveness standards, while clarifying the agency’s authority to consider research supporting previously approved targeted treatments. More information.

NORD supports this bipartisan bill, introduced in the US Senate, to advance the development of targeted drugs for patients with serious or life-threatening rare genetic diseases. The bill is intended to maintain FDA’s strong safety and effectiveness standards, while clarifying the agency’s authority to consider research supporting previously approved targeted treatments. More information.