Rare Diseases
Conference Coverage
Veterans Affairs Hailed as a ‘Bright Spot’ in ALS Care
Transdisciplinary collaboration is essential for maintaining an effective system.
Commentary
Unleashing Our Immune Response to Quash Cancer
“It’s astounding how devious cancer cells and tumor tissue can be.”
Latest News
Lichen Sclerosus: The Silent Genital Health Concern Often Missed
Lichen sclerosus, which causes pain, itching, and skin changes, most often effects the skin of the genital and anal regions.
Latest News
FDA Approves Topical Gel For Wounds Associated With JEB and DEB
The FDA has approved a topical gel containing birch triterpenes for the treatment of partial thickness wounds in patients 6 months and older with...
Commentary
Why Are Prion Diseases on the Rise?
Given these findings, it seems that a bit more surveillance for this rare but devastating condition is well merited.
News
Unexplained collapse unveils rare blood disorder
Acquired TTP often appears to arise in connection with either an immune trigger, such as a viral infection, or immune dysregulation associated...
News
FDA approves first tx for rare, deadly clotting disorder
First drug to treat TTP. a rare, lethal blood clotting disorder, has been greenlighted by the FDA.
News
Short steroid taper tested with tocilizumab for giant cell arteritis
Results from a pilot study examining a shortened prednisone taper of 8 weeks’ length rather than 26 weeks suggest it may be possible to reduce...
News
RNA therapeutics will ‘change everything’ in epilepsy
“We now have the potential to change the way genetic epilepsies are treated by addressing the underlying genetic cause of the disease instead of...
Commentary
Male patients with breast cancer: Special considerations and gender-specific concerns
Even the materials that we have are gender specific. I think those things all together can certainly contribute to a man feeling like a fish out...