Rare Diseases
Latest News
Oral Transmission of Chagas Disease Has Severe Effects
"A myth I would like to dispel is that Chagas disease is not being transmitted in the United States."
From the Journals
5 Interesting Neurology Studies
Latest News
National Rapid Genome Testing Program Benefits NICU Care
Rapid trio genome sequencing diagnosed 50% of the neonates with disease-causing genetic variants.
News from the FDA/CDC
FDA Approves 10th Humira Biosimilar, With Interchangeability
Adalimumab-ryvk (Simlandi) is the first adalimumab biosimilar in a high-concentration formulation to receive interchangeability status from the...
Latest News
Reduced-Dose Vaccines Protect Patients With HIV Against Mpox
The intradermal dose-saving vaccination is preferable to the subcutaneous route; patients with very low T cell counts may need a booster.
Latest News
Lichen Sclerosus: The Silent Genital Health Concern Often Missed
Lichen sclerosus, which causes pain, itching, and skin changes, most often effects the skin of the genital and anal regions.
Latest News
Study: Lifetime Cost of Vyjuvek Gene Therapy for DEB Could Be $15-$22 Million
"The wider indication granted by the FDA may lead to friction between payers on the one hand and patients and physicians on the other," the...
Latest News
Cutaneous lupus, dermatomyositis: Excitement growing around emerging therapies
Anticipation is growing for emerging therapies and their potential to provide relief to patients, said Anthony Fernandez, MD, PhD.
Latest News
Hair Loss in Children: How to Spot and Treat Different Causes
Most children with alopecia areata are healthy and do not need extensive screening laboratory testing. However, one exception is if thyroid...
Latest News
FDA Approves Topical Gel For Wounds Associated With JEB and DEB
The FDA has approved a topical gel containing birch triterpenes for the treatment of partial thickness wounds in patients 6 months and older with...
Commentary
Why Are Prion Diseases on the Rise?
Given these findings, it seems that a bit more surveillance for this rare but devastating condition is well merited.