Gene Therapy
Rare Disease Report 2024
Balancing Act: Weighing the Pros and Cons of Genetic Testing in Rare Diseases
While genetic testing may offer great potential for providing answers to patients and clinicians seeking insight into a rare disorder, the...
Feature
Time Warp: Fax Machines Still Common in Oncology Practice. Why?
Oncologists are among the many specialists across the country at the mercy of telecopiers.
Feature
Doctors Endorsing Products on X May Not Disclose Company Ties
Researchers review posts by physicians on X, looking for key words that might indicate that the posts were intended as endorsements of a product...
From the Journals
Most Targeted Cancer Drugs Lack Substantial Clinical Benefit
Researchers assess validity of the molecular targets and clinical benefits of genome-targeted cancer drugs approved in the United States from 2015...
From the Journals
Less Than 50% of Accelerated Approvals Show Clinical Benefit
Researchers review 46 cancer drugs granted accelerated approvals between 2013 and 2017.
Conference Coverage
Despite Few CNS Gene Therapies for Epilepsy, New Research Offers Hope
Sponsored Supplement
Fundamentals of Gene Therapy: Addressing Gaps in Physician Education
Conference Coverage
Genetic therapies bring change to neurology clinics
Advancements are set to alter the approach to some patients and inspire a demand for genetic counselors in neuromuscular clinics.
News
Why genetic testing may be our best shot at progress in Parkinson’s disease
A growing body of work has prompted researchers and drug developers to take a longer look at how genetics influence Parkinson’s disease risk and...
Conference Coverage
Gene therapy demonstrates modest success in genetic blindness
‘First step’ toward improvement in Leber hereditary optic neuropathy is maintained out to 4 years.
Conference Coverage
Survey identifies clinicians’ unease with genetic testing
A survey of Movement Disorders Society members identified a number of gaps in clinicians’ comfort levels with genetic testing for Parkinson’s...
Conference Coverage
Families face challenges of gene therapy
Patients and manufacturers continue on a learning curve to improve trial designs and patient experiences.