Anemia
News
FDA approves first drug for rare inherited anemia
First-ever drug for hemolytic anemia has been approved by the Food and Drug Administration.
News
FDA approves first-ever drug for cold agglutinin disease
The first drug to treat a rare anemia has been given the green light by the FDA.
News from the FDA/CDC
Voxelotor for sickle cell anemia now down to 4-year-olds
Conference Coverage
Telemedicine helps SCD patients survive COVID, but more need access
The second COVID-19 wave brought zero deaths and fewer complicated hospitalizations at the largest U.S. adult sickle cell disease center, but care...
Conference Coverage
Beta-thalassemia gene therapy achieves lasting transfusion independence
“Seeing the restoration of iron metabolism, it really takes us a step closer to really thinking the term ‘cure’ might truly apply.”
Opinion
Does optimal iron absorption include vitamin C?
Plus, how often should a patient with iron deficiency take oral iron supplementation?
From the Journals
Infusion centers may best EDs for treating sickle cell crises
At infusion centers, patients received pain medication an average of 70 minutes faster compared with patients treated in EDs.
From the Journals
Poloxamer 188 disappoints for painful SCD vaso-occlusive episodes, study showsteaser
Findings from a phase 3 trial failed to support those from a prior study showing that poloxamer 188 shortened painful vaso-occlusive episodes in...
News
FDA approves new treatment option for rare anemia
Pegcetacoplan (Empaveli) was approved as a treatment for paroxysmal nocturnal hemoglobinuria (PNH).
Commentary
Commentary: Functional assessment developed for older adults with sickle cell disease
Feature
Unique oral drug candidate designed to overcome sickle cell disease